Thank you for joining the Orphan Disease Center’s 10th Anniversary Celebration!
Session recordings are now available!
A New Era of Rare Disease Diagnostics & Therapeutics:
Penn’s Orphan Disease Center (ODC) is the first of its kind, a program dedicated to identifying promising therapies for oft-overlooked disorders and providing access to those therapies for patients of all populations. Led by world-renowned gene therapy pioneer Jim Wilson, the ODC has a track record of accelerating progress across a number of arenas, including infectious diseases, blood disorders, metabolic diseases, and neurologic disorders like Rett syndrome, CDKL5 deficiency disorder, and Duchenne muscular dystrophy. Join us as we take a look at where we have been – and where we are going.
Day 1
Wednesday, February 24th | 10:00 AM - 2:30 PM EST
Special Guest:
Francis S. Collins, MD, PhD
Director of the National Institutes of Health
Day 2
Thursday, February 25th | 10:00 AM - 3:00 PM EST
Special Guests:
Michael S. Brown, MD
Regental Professor, Molecular Genetics and Internal Medicine,
UT Southwestern
David Cameron
Former Prime Minister of the United Kingdom
President of Alzheimer's Research UK
&
Janet Woodcock, MD
Acting Commissioner,
US Food & Drug Administration
In the News:
PHILLY’S POTENTIAL TO CHANGE THE WORLD: Penn’s Orphan Disease Center turns 10 this year. Its promise for Philadelphia goes well beyond science
THE PHILADELPHIA CITIZEN BY AJAY RAJU FEB. 17, 2021
“This reality is one that Wilson and the ODC have fully embraced, recognizing that while the essential science behind developing cures for the world’s toughest diseases may happen in the monastic confines of a laboratory, the funding, promotion and scalable delivery of those cures demands an all-hands-on-deck effort.”